Thalassemia is a type of hereditary blood disorder in which an abnormal form of hemoglobin is produced by the human body. It leads to destruction of a large number of blood cells, resulting in anemia. Thalassemia is a genetic disorder and it is caused by genetic mutation or deletion of a specific gene fragment. If only one parent is the carrier of the gene, the offspring may develop thalassemia minor. If both parents are carriers of the disease, there is a possibility of developing a serious form of the disease. There are three types of thalassemia viz. beta thalassemia, alpha thalassemia, and thalassemia minor. The treatment of the disorder depends on its severity and type. In beta thalassemia, the body cannot produce beta globulin. The patients with beta and those with alpha thalassemia manifest more severe symptoms as compared to thalassemia minor. Some of the common symptoms are bone deformities, dark urine, pale skin, and excessive fatigue.

The global thalassemia therapeutics market is estimated to expand at a significant rate during the forecast period. According to the WHO, prevalence of the disease is high in malaria-endemic regions. In some regions, prevalence of the disease has reason to become a public concern. This is one of the major factors likely to drive the global thalassemia therapeutics market during the forecast period. Rise in awareness, advancements in technology such as stem cell therapy, increase in health care expenditure, and promising pipeline are some of the other factors expected to drive the global thalassemia therapeutics market between 2017 and 2025. Furthermore, government initiatives to create awareness about thalassemia are expected to drive the market in the next few years. An example of such initiatives is Registry & Surveillance System for Hemoglobinopathies (RuSH), which collects specific information from thalassemia patients. It was started in collaboration with Centers for Disease Control and Prevention (CDC) in 2010. However, high cost of treatment, lack of awareness in some developing countries, and lack of medical coverage can restrain the thalassemia therapeutics market during the forecast period.

The global thalassemia therapeutics market can be segmented based on type, drug class, distribution channel, and region. Based on type, the market can be divided into beta thalassemia, alpha thalassemia, and thalassemia minor. The beta thalassemia segment is expected to hold the leading share of the market from 2017 to 2025, due to its higher prevalence compared to other types and high severity. Based on drug class, the global thalassemia therapeutics market can be classified into antimetabolites, antidotes, chelating agents, and others. Based on distribution channel, the market has been divided into retail stores, drug stores and e-commerce. The e-commerce segment is expected to hold a significant market share by 2025, owing to user convenience.

Geographically, the global thalassemia therapeutics market has been divided into North America, Asia Pacific, Latin America, Europe, and Middle East & Africa. North America is anticipated to dominate the global market during the forecast period. Risen awareness and increased government efforts are some of the important factors driving the market in the region during the forecast period. Furthermore, technological advancements and rise in per capita health care expenditure are other factors augmenting the market in the region. Europe is expected to hold a significant share of the global market during the forecast period, followed by North America. Factors responsible for growth of the market in Europe are high prevalence of hemoglobinopathies (such as thalassemia and sickle cell anemia) and awareness among people about disorders. The market in Asia Pacific is anticipated to register a rapid growth rate during the forecast period. Asia Pacific is a highly attractive market for thalassemia therapeutics, due to high prevalence of thalassemia in the region, rising awareness among people, and entry of new players in the market in the region.

Many players operating in the global thalassemia therapeutics market are adopting strategies such as new product development, promising pipeline, commercialization, and geographical expansion. Some of the prominent players operating in the global thalassemia therapeutics market are Lonza Group Ltd, Bluebird Bio, Acceleron Pharma, Inc., Sangamo Bioscience, and Kiadis Pharma.

This study by TMR is all-encompassing framework of the dynamics of the market. It mainly comprises critical assessment of consumers' or customers' journeys, current and emerging avenues, and strategic framework to enable CXOs take effective decisions.

Our key underpinning is the 4-Quadrant Framework EIRS that offers detailed visualization of four elements:

  • Customer Experience Maps
  • Insights and Tools based on data-driven research
  • Actionable Results to meet all the business priorities
  • Strategic Frameworks to boost the growth journey

The study strives to evaluate the current and future growth prospects, untapped avenues, factors shaping their revenue potential, and demand and consumption patterns in the global market by breaking it into region-wise assessment.

The following regional segments are covered comprehensively:

  • North America
  • Asia Pacific
  • Europe
  • Latin America
  • The Middle East and Africa

The EIRS quadrant framework in the report sums up our wide spectrum of data-driven research and advisory for CXOs to help them make better decisions for their businesses and stay as leaders.

Below is a snapshot of these quadrants.

1. Customer Experience Map

The study offers an in-depth assessment of various customers’ journeys pertinent to the market and its segments. It offers various customer impressions about the products and service use. The analysis takes a closer look at their pain points and fears across various customer touchpoints. The consultation and business intelligence solutions will help interested stakeholders, including CXOs, define customer experience maps tailored to their needs. This will help them aim at boosting customer engagement with their brands.

2. Insights and Tools

The various insights in the study are based on elaborate cycles of primary and secondary research the analysts engage with during the course of research. The analysts and expert advisors at TMR adopt industry-wide, quantitative customer insights tools and market projection methodologies to arrive at results, which makes them reliable. The study not just offers estimations and projections, but also an uncluttered evaluation of these figures on the market dynamics. These insights merge data-driven research framework with qualitative consultations for business owners, CXOs, policy makers, and investors. The insights will also help their customers overcome their fears.

3. Actionable Results

The findings presented in this study by TMR are an indispensable guide for meeting all business priorities, including mission-critical ones. The results when implemented have shown tangible benefits to business stakeholders and industry entities to boost their performance. The results are tailored to fit the individual strategic framework. The study also illustrates some of the recent case studies on solving various problems by companies they faced in their consolidation journey.

4. Strategic Frameworks

The study equips businesses and anyone interested in the market to frame broad strategic frameworks. This has become more important than ever, given the current uncertainty due to COVID-19. The study deliberates on consultations to overcome various such past disruptions and foresees new ones to boost the preparedness. The frameworks help businesses plan their strategic alignments for recovery from such disruptive trends. Further, analysts at TMR helps you break down the complex scenario and bring resiliency in uncertain times.

The report sheds light on various aspects and answers pertinent questions on the market. Some of the important ones are:

1. What can be the best investment choices for venturing into new product and service lines?

2. What value propositions should businesses aim at while making new research and development funding?

3. Which regulations will be most helpful for stakeholders to boost their supply chain network?

4. Which regions might see the demand maturing in certain segments in near future?

5. What are the some of the best cost optimization strategies with vendors that some well-entrenched players have gained success with?

6. Which are the key perspectives that the C-suite are leveraging to move businesses to new growth trajectory?

7. Which government regulations might challenge the status of key regional markets?

8. How will the emerging political and economic scenario affect opportunities in key growth areas?

9. What are some of the value-grab opportunities in various segments?

10. What will be the barrier to entry for new players in the market?

Note: Although care has been taken to maintain the highest levels of accuracy in TMR’s reports, recent market/vendor-specific changes may take time to reflect in the analysis.

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Thalassemia Therapeutics Market

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