The report details an exhaustive account of the global fragile X syndrome market along with numerous associated factors. Some of these factors that are included in the report are drivers, restraints, competitive analysis, latest trends and opportunities, geographical outlook, and many other aspects. The study covered in the fragile X syndrome market’s report spans a forecast period from 2018 to 2026. From an overall perspective, the report is expected to exist as a valuable insight to businesses which are already operating in the global fragile X syndrome market, as well for those who intend to newly establish themselves in this environment. 

Fragile X syndrome is a genetic disorder that leads to various developmental hitches including learning disabilities and cognitive impairment. Men are more often affected by this disorder than women.

In case of affected individuals, there is delayed development of speech and language by age 2. Majority of men suffering with fragile X syndrome suffer from mild to moderate intellectual disability compared to one-third women. Children suffering with fragile X syndrome could also show anxiety and hyperactive behavior such as fidgeting or impulsive behavior. These children could also suffer from reduced ability to maintain attention and exhibit difficulty in concentrating on specific tasks. Around one-third of individuals suffering with fragile X syndrome have some symptoms of autism spectrum disorders that disturb communication as well as social interaction. About 15% men and 5% women suffering from fragile X syndrome can experience seizures. These are key factors pushing towards more growth in the global fragile X syndrome market 

Prevalence of fragile X syndrome is rising owing to lack of awareness among people about genetic disorders that result in mutations in DNA. Smoking, consumption of alcohol during pregnancy, and hereditary disorders increase the prevalence of fragile X syndrome. The pipeline of global fragile X syndrome market is anticipated to expand rapidly during the forecast period owing to increase in focus of pharmaceuticals & biotechnology companies on conducting research programs to develop effective therapeutic agents for the treatment of the syndrome.

The global fragile X syndrome market can be segmented based on product, end-user, and region. In terms of product, the global market can be classified into ACT-01, AMO-01, ANAVEX-273, and AUT-00206. Based on end-user, the global fragile X syndrome market can be divided into clinics, hospitals, and research centers. In terms of region, the global market can be segmented into North America, Europe, Asia Pacific, Latin America, and Middle East & Africa. 

Based on pipeline analysis of fragile X syndrome, various therapeutic agents or drugs are available under the pipeline segment of various pharmaceutical companies in the global fragile X syndrome market. OV-101 is an agent being developed by Ovid therapeutics, Inc., and is in phase I of clinical trials. This drug, OV-101, has an oral route of administration, and targets GABA-A (gamma-aminobutyric acid) receptor delta (GABRD) and acts as an agonist to GABA-A receptor delta (GABRD). A drug developed by Bellus Health, Inc. in collaboration with AMO Pharmaceutical under the name AMO-01 also aims to treat fragile X syndrome in the global fragile X syndrome market. Presently, it is in phase II stage of clinical trials. AMO-01 is a small drug molecule that targets peripheral benzodiazepine receptor (PBR). Ganaxolone is a drug developed by Marinus Pharmaceutical and is currently in phase II clinical trials in the global fragile X syndrome market. It is a small molecule, orally administered drug that modulates gamma-aminobutyric acid (GABA). NNZ-2566 is another drug developed by Neuren Pharmaceuticals which demonstrates the efficacy to treat Rett syndrome as well as fragile X syndrome in the global fragile X syndrome market. NNZ-2566 is in phase II stage of clinical trials and acts as an inhibitor of cytokines activity in the human body. 

Companies having drugs in their pipeline in global fragile X syndrome market for the treatment of fragile X syndrome include Anavex Life Sciences Corp., Ovid Therapeutics, Neuren Pharmaceuticals, Eli Lilly and Company, Bellus Health, Inc., AMO Pharma, Marinus Pharmaceuticals, Inc., Kareus Therapeutics. SA, and Zynerba Pharmaceuticals, Inc.

This study by TMR is all-encompassing framework of the dynamics of the market. It mainly comprises critical assessment of consumers' or customers' journeys, current and emerging avenues, and strategic framework to enable CXOs take effective decisions.

Our key underpinning is the 4-Quadrant Framework EIRS that offers detailed visualization of four elements:

  • Customer Experience Maps
  • Insights and Tools based on data-driven research
  • Actionable Results to meet all the business priorities
  • Strategic Frameworks to boost the growth journey

The study strives to evaluate the current and future growth prospects, untapped avenues, factors shaping their revenue potential, and demand and consumption patterns in the global market by breaking it into region-wise assessment.

The following regional segments are covered comprehensively:

  • North America
  • Asia Pacific
  • Europe
  • Latin America
  • The Middle East and Africa

The EIRS quadrant framework in the report sums up our wide spectrum of data-driven research and advisory for CXOs to help them make better decisions for their businesses and stay as leaders.

Below is a snapshot of these quadrants.

1. Customer Experience Map

The study offers an in-depth assessment of various customers’ journeys pertinent to the market and its segments. It offers various customer impressions about the products and service use. The analysis takes a closer look at their pain points and fears across various customer touchpoints. The consultation and business intelligence solutions will help interested stakeholders, including CXOs, define customer experience maps tailored to their needs. This will help them aim at boosting customer engagement with their brands.

2. Insights and Tools

The various insights in the study are based on elaborate cycles of primary and secondary research the analysts engage with during the course of research. The analysts and expert advisors at TMR adopt industry-wide, quantitative customer insights tools and market projection methodologies to arrive at results, which makes them reliable. The study not just offers estimations and projections, but also an uncluttered evaluation of these figures on the market dynamics. These insights merge data-driven research framework with qualitative consultations for business owners, CXOs, policy makers, and investors. The insights will also help their customers overcome their fears.

3. Actionable Results

The findings presented in this study by TMR are an indispensable guide for meeting all business priorities, including mission-critical ones. The results when implemented have shown tangible benefits to business stakeholders and industry entities to boost their performance. The results are tailored to fit the individual strategic framework. The study also illustrates some of the recent case studies on solving various problems by companies they faced in their consolidation journey.

4. Strategic Frameworks

The study equips businesses and anyone interested in the market to frame broad strategic frameworks. This has become more important than ever, given the current uncertainty due to COVID-19. The study deliberates on consultations to overcome various such past disruptions and foresees new ones to boost the preparedness. The frameworks help businesses plan their strategic alignments for recovery from such disruptive trends. Further, analysts at TMR helps you break down the complex scenario and bring resiliency in uncertain times.

The report sheds light on various aspects and answers pertinent questions on the market. Some of the important ones are:

1. What can be the best investment choices for venturing into new product and service lines?

2. What value propositions should businesses aim at while making new research and development funding?

3. Which regulations will be most helpful for stakeholders to boost their supply chain network?

4. Which regions might see the demand maturing in certain segments in near future?

5. What are the some of the best cost optimization strategies with vendors that some well-entrenched players have gained success with?

6. Which are the key perspectives that the C-suite are leveraging to move businesses to new growth trajectory?

7. Which government regulations might challenge the status of key regional markets?

8. How will the emerging political and economic scenario affect opportunities in key growth areas?

9. What are some of the value-grab opportunities in various segments?

10. What will be the barrier to entry for new players in the market?

With a robust experience in creating exceptional market reports, Transparency Market Research has emerged as one of the trusted market research companies among a large number of stakeholders and CXOs. Every report at Transparency Market Research goes through rigorous research activity in every aspect. The researchers at TMR keep a close watch on the market and extract beneficial growth-boosting points. These points help the stakeholders to strategize their business plans accordingly.

TMR researchers conduct exhaustive qualitative and quantitative research. This research involves taking inputs from the experts in the market, focused attention on recent developments, and others. This method of research makes TMR stand out from other market research firms.

Here's how Transparency Market Research helps the stakeholders and CXOs through the reports:

Inculcation and Evaluation of Strategic Collaborations: The TMR researchers analyze recent strategic activities like mergers, acquisitions, partnerships, collaborations, and joint ventures. All the information is compiled and included in the report.

Perfect Market Size Estimations: The report analyzes the demographics, growth potential, and capability of the market through the forecast period. This factor leads to the estimation of the market size and also provides an outline about how the market will retrieve growth during the assessment period.

Investment Research: The report focuses on the ongoing and upcoming investment opportunities across a particular market. These developments make the stakeholders aware of the current investment scenario across the market.

Note: Although care has been taken to maintain the highest levels of accuracy in TMR’s reports, recent market/vendor-specific changes may take time to reflect in the analysis.

Custom Market Research Services

TMR offers custom market research services that help clients to get information on their business scenario required where syndicated solutions are not enough.

REQUEST CUSTOMIZATION

Fragile X Syndrome Market

Pre Book